Medications for Spinal Muscular Atrophy

6 results
  • estradiol

    (estradiol)
    Preferred Pharmaceuticals Inc.
    Estradiol transdermal system is indicated for treating moderate to severe vasomotor symptoms and vulvar/vaginal atrophy due to menopause, hypoestrogenism from various causes, and preventing postmenopausal osteoporosis, ideally after evaluating other treatment options first.
  • estradiol transdermal system

    (Estradiol)
    Sandoz Inc
    The Estradiol Transdermal System is indicated for treating moderate to severe vasomotor symptoms and vulvar/vaginal atrophy due to menopause, hypoestrogenism from various causes, and prevention of postmenopausal osteoporosis, with specific limitations for certain conditions.
  • estring

    (estradiol)
    Pfizer Laboratories Div Pfizer Inc
    ESTRING is indicated for treating moderate to severe vulvar and vaginal atrophy symptoms associated with menopause.
  • evrysdi

    (Risdiplam)
    Genentech Inc.
    EVRYSDI is indicated for the treatment of spinal muscular atrophy (SMA) in both pediatric and adult patients.
  • spinraza

    (Nusinersen)
    Biogen
    SPINRAZA is indicated for the treatment of spinal muscular atrophy (SMA) in both pediatric and adult patients.
  • zolgensma

    (onasemnogene abeparvovec-xioi)
    Novartis Gene Therapies, Inc.
    ZOLGENSMA is a gene therapy for pediatric patients under 2 years old with spinal muscular atrophy (SMA) caused by bi-allelic mutations in the SMN1 gene. Its safety for repeat use or in advanced SMA cases is not established.