Medications for Transfusion Dependent Thalassaemia Beta

1 result
  • casgevy

    (Exagamglogene Autotemcel)
    Vertex Pharmaceuticals Incorporated
    Casgevy is used to treat patients aged 2 and older with sickle cell disease (SCD) that causes recurring pain crises, or transfusion-dependent beta-thalassemia (TDT), a condition requiring regular blood transfusions.