dojolvi
(Triheptanoin)Ultragenyx Pharmaceutical Inc.
Usage: DOJOLVI is indicated for providing calories and fatty acids to adult and pediatric patients with molecularly confirmed long-chain fatty acid oxidation disorders (LC-FAOD).
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mepsevii
(vestronidase alfa)Ultragenyx Pharmaceutical Inc.Usage: MEPSEVII is indicated for treating Mucopolysaccharidosis VII (MPS VII, Sly syndrome) in pediatric and adult patients. Note that its effects on central nervous system manifestations of MPS VII are not yet established.